Recent progress in the understanding and treatment of transthyretin amyloidosis.

What is known and objective Transthyretin ( TTR) is a representative amyloidogenic protein in humans. Rate-limiting tetramer dissociation and rapid monomer misfolding and misassembly of variant TTR result in autosomal dominant familial amyloidosis. Analogous misfolding of wild-type TTR results in se...

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Publicado en:Journal of Clinical Pharmacy & Therapeutics Vol. 39; no. 3; pp. 225 - 234
Autor principal: Sekijima, Y.
Formato: pictorial review tables/charts Journal Article
Publicado: Wiley-Blackwell Jun2014
Acceso en línea:Ver este registro en EBSCOhost