Endocrine and Bone Complications in β-Thalassemia Intermedia: Current Understanding and Treatment.
Thalassemia intermedia (TI), also known as nontransfusion dependent thalassemia (NTDT), is a type of thalassemia where affected patients do not require lifelong regular transfusions for survival but may require occasional or even frequent transfusions in certain clinical settings and for defined per...
| Publicado en: | BioMed Research International Vol. 2015; pp. 1 - 10 |
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| Autores principales: | , , , |
| Formato: | review tables/charts Journal Article |
| Publicado: |
Wiley-Blackwell
3/9/2015
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| Acceso en línea: | Ver este registro en EBSCOhost |
| fields | @attributes: recordID: 1 pdfLink: plink: https://search.ebscohost.com/login.aspx?direct=true&db=ccm&AN=109273604&site=ehost-live header: @attributes: shortDbName: ccm uiTerm: 109273604 longDbName: CINAHL Complete uiTag: AN controlInfo: bkinfo: dissinfo: jinfo: jid: 23146133 FT2T jtl: BioMed Research International issn: 23146133 maglogo: N pubinfo: dt: 3/9/2015 vid: 2015 pid: 480 pub: Wiley-Blackwell place: Malden, Massachusetts artinfo: ui: 109273604 109273604 109273604 10.1155/2015/813098 109273604 ppf: 1 ppct: 9 formats: fmt: @attributes: type: P tig: atl: Endocrine and Bone Complications in β-Thalassemia Intermedia: Current Understanding and Treatment. aug: au: Inati, Adlette Noureldine, MohammadHassan A. Mansour, Anthony Abbas, Hussein A. affil: Department of Pediatrics, Rafic Hariri University Hospital, Beirut, Lebanon sug: subj: beta-Thalassemia Diagnosis Endocrine Diseases Diagnosis Bone Diseases Diagnosis beta-Thalassemia Physiopathology beta-Thalassemia Therapy Iron Blood Iron Physiology Endocrinology Iron Overload Diagnosis Iron Overload Therapy Iron Overload Complications Puberty Hypogonadism Diabetes Mellitus Glucose Intolerance Female Hyperlipidemia Osteoporosis Diagnosis Bone Marrow Physiology Female ab: Thalassemia intermedia (TI), also known as nontransfusion dependent thalassemia (NTDT), is a type of thalassemia where affected patients do not require lifelong regular transfusions for survival but may require occasional or even frequent transfusions in certain clinical settings and for defined periods of time. NTDT encompasses three distinct clinical forms: β-thalassemia intermedia (β-TI), Hb E/β-thalassemia, and α-thalassemia intermedia (Hb H disease). Over the past decade, our understanding of the molecular features, pathophysiology, and complications of NTDT particularly β-TI has increased tremendously but data on optimal treatment of disease and its various complications are still lacking. In this paper, we shall review a group of commonly encountered complications in β-TI, mainly endocrine and bone complications. pubtype: Academic Journal doctype: review tables/charts Journal Article ougenre: Article language: English refInfo: holdings: @attributes: islocal: N |
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