The novel fungal CYP51 inhibitor VT-1598 is efficacious alone and in combination with liposomal amphotericin B in a murine model of cryptococcal meningitis.

Objectives: Annual global deaths from cryptococcal meningitis (CM) are estimated at 180 000 and mortality is as high as 30%, even with optimal therapy. VT-1598 is a novel fungal CYP51 inhibitor with potent intrinsic antifungal activity against Cryptococcus. We report here VT-1598's in vivo antifunga...

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Publicado en:Journal of Antimicrobial Chemotherapy (JAC) Vol. 73; no. 10; pp. 2815 - 2823
Autores principales: Garvey, E P, Sharp, A D, Warn, P A, Yates, C M, Schotzinger, R J
Formato: research tables/charts Journal Article
Publicado: Oxford University Press / USA Oct2018
Acceso en línea:Ver este registro en EBSCOhost
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      dt: Oct2018
      vid: 73
      iid: 10
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      pub: Oxford University Press / USA
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        10.1093/jac/dky242
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        atl: The novel fungal CYP51 inhibitor VT-1598 is efficacious alone and in combination with liposomal amphotericin B in a murine model of cryptococcal meningitis.
      aug:
        au:
          Garvey, E P
          Sharp, A D
          Warn, P A
          Yates, C M
          Schotzinger, R J
        affil: Viamet Pharmaceuticals, Inc., Durham, NC, USA
      sug:
        subj:
          Antifungal Agents Administration and Dosage
          Enzyme Inhibitors Administration and Dosage
          Meningitis, Cryptococcal Drug Therapy
          Amphotericin B Administration and Dosage
          Amphotericin B Pharmacodynamics
          Administration, Oral
          Antifungal Agents Pharmacodynamics
          Models, Biological
          Cryptococcus
          Colony Count, Microbial
          Animal Studies
          Treatment Outcomes
          Microbial Culture and Sensitivity Tests
          Survival Analysis
          Drug Therapy, Combination Methods
          Cryptococcus Drug Effects
          Enzyme Inhibitors Pharmacodynamics
          Mice
          Validation Studies
          Comparative Studies
          Evaluation Research
          Multicenter Studies
      ab: Objectives: Annual global deaths from cryptococcal meningitis (CM) are estimated at 180 000 and mortality is as high as 30%, even with optimal therapy. VT-1598 is a novel fungal CYP51 inhibitor with potent intrinsic antifungal activity against Cryptococcus. We report here VT-1598's in vivo antifungal activity in a murine model of CM.Methods: Single-dose plasma and brain pharmacokinetics in mice and MIC for Cryptococcus neoformans H99 were determined prior to efficacy studies. Short-course monotherapy and combination doses were explored with the endpoint of brain fungal burden. A survival study was also conducted using monotherapy treatment with fungal burden measured after a 6 day drug washout.Results: Oral doses of VT-1598 had good plasma and brain exposure and resulted in significant (P < 0.0001) and dose-dependent reductions in brain fungal burden, reaching a 6 log10 reduction. Unlike either positive drug control (fluconazole or liposomal amphotericin B), both mid and high doses of VT-1598 reduced fungal burden to below levels measured at the start of treatment. When VT-1598 was dosed in the survival study, no VT-1598-treated animal succumbed to the infection. Whereas fluconazole showed a 2.5 log10 increase in fungal burden after the 6 day washout, the VT-1598 mid- and high-dose animals showed almost no regrowth (<0.5 log10). In a separate fungal burden study using suboptimal doses of VT-1598 and liposomal amphotericin B to probe for combination effects, each combination had a positive effect relative to corresponding monotherapies.Conclusions: These pre-clinical in vivo data strongly support clinical investigation of VT-1598 as a novel therapy for this lethal infection.
      pubtype: Academic Journal
      doctype:
        research
        tables/charts
        Journal Article
      ougenre: Article
    language: English
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