Cost-effectiveness analysis of three algorithms for diagnosing primary ciliary dyskinesia: a simulation study.

Background: Primary Ciliary Dyskinesia (PCD) diagnosis relies on a combination of tests which may include (a) nasal Nitric Oxide (nNO), (b) High Speed Video Microscopy (HSVM) and (c) Transmission Electron Microscopy (TEM). There is variability in the availability of these tests and lack of universal...

Descripción completa

Detalles Bibliográficos
Publicado en:Orphanet Journal of Rare Diseases Vol. 14; no. 1
Autores principales: Kouis, Panayiotis, Papatheodorou, Stefania I., Middleton, Nicos, Giallouros, George, Kyriacou, Kyriacos, Cohen, Joshua T., Evans, John S., Yiallouros, Panayiotis K.
Formato: research Journal Article
Publicado: BioMed Central 6/13/2019
Acceso en línea:Ver este registro en EBSCOhost
fields @attributes:
  recordID: 1
pdfLink:
plink: https://search.ebscohost.com/login.aspx?direct=true&db=ccm&AN=136999590&site=ehost-live
header:
  @attributes:
    shortDbName: ccm
    uiTerm: 136999590
    longDbName: CINAHL Complete
    uiTag: AN
  controlInfo:
    bkinfo:
    dissinfo:
    jinfo:
      jid:
        17501172
        38NP
      jtl: Orphanet Journal of Rare Diseases
      issn: 17501172
      maglogo: N
    pubinfo:
      dt: 6/13/2019
      vid: 14
      iid: 1
      pid: 24147
      pub: BioMed Central
    artinfo:
      ui:
        136999590
        136999590
        NLM31196140
        136999590
        10.1186/s13023-019-1116-3
        NLM31196140
        136999590
      ppct: 1
      formats:
      tig:
        atl: Cost-effectiveness analysis of three algorithms for diagnosing primary ciliary dyskinesia: a simulation study.
      aug:
        au:
          Kouis, Panayiotis
          Papatheodorou, Stefania I.
          Middleton, Nicos
          Giallouros, George
          Kyriacou, Kyriacos
          Cohen, Joshua T.
          Evans, John S.
          Yiallouros, Panayiotis K.
        affil: Respiratory Physiology Laboratory, Medical School, University of Cyprus, Nicosia, Cyprus
      sug:
        subj:
          Algorithms
          Ciliary Motility Disorders Diagnosis
          Ciliary Motility Disorders Physiopathology
          Cost Benefit Analysis
          Sensitivity and Specificity
          Female
          Ciliary Motility Disorders Metabolism
          Quality of Life
          Male
          Human
          Nitric Oxide Metabolism
          Microscopy, Electron
          Validation Studies
          Comparative Studies
          Evaluation Research
          Multicenter Studies
          Ferrans and Powers Quality of Life Index
          Female
          Male
      ab: Background: Primary Ciliary Dyskinesia (PCD) diagnosis relies on a combination of tests which may include (a) nasal Nitric Oxide (nNO), (b) High Speed Video Microscopy (HSVM) and (c) Transmission Electron Microscopy (TEM). There is variability in the availability of these tests and lack of universal agreement whether diagnostic tests should be performed in sequence or in parallel. We assessed three combinations of tests for PCD diagnosis and estimated net sensitivity and specificity as well as cost-effectiveness (CE) and incremental cost-effectiveness (ICE) ratios.Methods and Results: A hypothetical initial population of 1000 referrals (expected 320 PCD patients) was followed through a probabilistic decision analysis model which was created to assess the CE of three diagnostic algorithms (a) nNO + TEM in sequence, (b) nNO + HSVM in sequence and (c) nNO/HSVM in parallel followed, in cases with conflicting results, by confirmatory TEM (nNO/HSVM+TEM). Number of PCD patients identified, CE and ICE ratios were calculated using Monte Carlo simulations. Out of 320 expected PCD patients, 313 were identified by nNO/HSVM+TEM, 274 with nNO + HSVM and 198 with nNO + TEM. The nNO/HSVM+TEM had the highest mean annual cost (€209 K) followed by nNO + TEM (€150 K) and nNO + HSVM (€136 K). The nNO + HSVM algorithm dominated the nNO + TEM algorithm (less costly and more effective). The ICE ratio for nNO/HSVM+TEM was €2.1 K per additional PCD patient identified.Conclusions: The diagnostic algorithm (nNO/HSVM+TEM) with parallel testing outperforms algorithms with tests in sequence. These findings, can inform the dialogue on the development of evidence-based guidelines for PCD diagnostic testing. Future research in understudied aspects of the disease, such as PCD-related quality of life and PCD-associated costs, is needed to help the better implementation of these guidelines across various healthcare systems.
      pubtype: Academic Journal
      doctype:
        research
        Journal Article
      ougenre: Article
    language: English
    refInfo:
    holdings:
      @attributes:
        islocal: N