Reduction of recruitment costs in preclinical AD trials: validation of automatic pre-screening algorithm for brain amyloidosis.

We propose a method for recruiting asymptomatic Amyloid positive individuals in clinical trials, using a two-step process. We first select during a pre-screening phase a subset of individuals which are more likely to be amyloid positive based on the automatic analysis of data acquired during routine...

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Publicado en:Statistical Methods in Medical Research Vol. 29; no. 1; pp. 151 - 165
Autores principales: Ansart, Manon, Epelbaum, Stéphane, Gagliardi, Geoffroy, Colliot, Olivier, Dormont, Didier, Dubois, Bruno, Hampel, Harald, Durrleman, Stanley
Formato: research Journal Article
Publicado: Sage Publications Inc. Jan2020
Acceso en línea:Ver este registro en EBSCOhost
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      dt: Jan2020
      vid: 29
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      pub: Sage Publications Inc.
      place: Thousand Oaks, California
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        atl: Reduction of recruitment costs in preclinical AD trials: validation of automatic pre-screening algorithm for brain amyloidosis.
      aug:
        au:
          Ansart, Manon
          Epelbaum, Stéphane
          Gagliardi, Geoffroy
          Colliot, Olivier
          Dormont, Didier
          Dubois, Bruno
          Hampel, Harald
          Durrleman, Stanley
        affil: Institut du Cerveau et de la Moelle épinière, ICM, Inserm, U 1127, CNRS, UMR 7225, Sorbonne Université, Paris, France
      sug:
        subj:
          Patient Selection
          Alzheimer's Disease
          Tomography, Emission-Computed
          Algorithms
          Health Screening Economics
          Amyloidosis
          Prospective Studies
          Human
          Clinical Trials
          France
          Disease Progression
          Models, Statistical
          Comparative Studies
          Multicenter Studies
          Evaluation Research
          Validation Studies
      ab: We propose a method for recruiting asymptomatic Amyloid positive individuals in clinical trials, using a two-step process. We first select during a pre-screening phase a subset of individuals which are more likely to be amyloid positive based on the automatic analysis of data acquired during routine clinical practice, before doing a confirmatory PET-scan to these selected individuals only. This method leads to an increased number of recruitments and to a reduced number of PET-scans, resulting in a decrease in overall recruitment costs. We validate our method on three different cohorts, and consider five different classification algorithms for the pre-screening phase. We show that the best results are obtained using solely cognitive, genetic and socio-demographic features, as the slight increased performance when using MRI or longitudinal data is balanced by the cost increase they induce. We show that the proposed method generalizes well when tested on an independent cohort, and that the characteristics of the selected set of individuals are identical to the characteristics of a population selected in a standard way. The proposed approach shows how Machine Learning can be used effectively in practice to optimize recruitment costs in clinical trials.
      pubtype: Academic Journal
      doctype:
        research
        Journal Article
      ougenre: Article
    language: English
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