Long-term complications of systemic oxalosis in children—a retrospective single-center cohort study.

Background: Systemic oxalosis is a severe complication seen in primary hyperoxaluria type I patients with kidney failure. Deposition of insoluble calcium oxalate crystals in multiple organs leads to significant morbidity and mortality. Methods: We describe a retrospective cohort of 11 patients with...

Descripción completa

Detalles Bibliográficos
Publicado en:Pediatric Nephrology Vol. 36; no. 10; pp. 3123 - 3133
Autores principales: Ben-Shalom, Efrat, Cytter-Kuint, Ruth, Rinat, Choni, Becker-Cohen, Rachel, Tzvi-Behr, Shimrit, Goichberg, Jenny, Peles, Vardit, Frishberg, Yaacov
Formato: diagnostic images pictorial research tables/charts Journal Article
Publicado: Springer Nature Oct2021
Acceso en línea:Ver este registro en EBSCOhost
fields @attributes:
  recordID: 1
pdfLink:
plink: https://search.ebscohost.com/login.aspx?direct=true&db=ccm&AN=152503174&site=ehost-live
header:
  @attributes:
    shortDbName: ccm
    uiTerm: 152503174
    longDbName: CINAHL Complete
    uiTag: AN
  controlInfo:
    bkinfo:
    dissinfo:
    jinfo:
      jid:
        0931041X
        EF1
      jtl: Pediatric Nephrology
      issn: 0931041X
      maglogo: N
    pubinfo:
      dt: Oct2021
      vid: 36
      iid: 10
      pid: 237
      pub: Springer Nature
      place: New York, New York
    artinfo:
      ui:
        152503174
        149008633
        152503174
        152503174
        10.1007/s00467-021-05002-1
        152503174
      ppf: 3123
      ppct: 10
      formats:
        fmt:
          @attributes:
            type: P
      tig:
        atl: Long-term complications of systemic oxalosis in children—a retrospective single-center cohort study.
      aug:
        au:
          Ben-Shalom, Efrat
          Cytter-Kuint, Ruth
          Rinat, Choni
          Becker-Cohen, Rachel
          Tzvi-Behr, Shimrit
          Goichberg, Jenny
          Peles, Vardit
          Frishberg, Yaacov
        affil: Institute of Pediatric Nephrology, Shaare Zedek Medical Center, 12 Shmuel Bait St., 9103102, Jerusalem, Israel
      sug:
        subj:
          Metabolic Diseases Complications
          Dialysis
          Kidney Physiology
          Oxalic Acids Metabolism
          Metabolic Diseases Therapy
          Human
          Retrospective Design
          Child
          Dialysis Centers
          Record Review
          Descriptive Statistics
          Male
          Female
          Bone Diseases
          Fractures
          Kidney Transplantation
          Liver Transplantation
          Child: 6-12 years
          Male
          Female
      ab: Background: Systemic oxalosis is a severe complication seen in primary hyperoxaluria type I patients with kidney failure. Deposition of insoluble calcium oxalate crystals in multiple organs leads to significant morbidity and mortality. Methods: We describe a retrospective cohort of 11 patients with systemic oxalosis treated at our dialysis unit from 1982 to 1998 (group 1) and 2007–2019 (group 2). Clinical and demographic data were collected from medical records. Imaging studies were only available for patients in group 2 (n = 5). Results: Median age at dialysis initiation was 6.1 months (IQR 4–21.6), 64% were male. Dialysis modality was mostly peritoneal dialysis in group 1 and daily hemodialysis in group 2. Bone disease was the first manifestation of systemic oxalosis, starting with the appearance of sclerotic bands (mean 166 days, range 1–235), followed by pathological fractures in long bones (mean 200.4 days, range 173–235 days). Advanced disease was characterized by vertebral fractures with resulting kyphosis, worsening splenomegaly, and adynamic bone disease. Two patients developed pulmonary hypertension, 4 and 8 months prior to their death. Four of 11 patients developed hypothyroidism 0–60 months after dialysis initiation. Only one patient survived after a successful liver–kidney transplantation. Four patients died after liver or liver–kidney transplantation. Conclusions: This is the first comprehensive description of the natural history of pediatric systemic oxalosis. We hope that our findings will provide basis for a quantitative severity score in future, larger studies.
      pubtype: Academic Journal
      doctype:
        diagnostic images
        pictorial
        research
        tables/charts
        Journal Article
      ougenre: Article
    language: English
    refInfo:
    holdings:
      @attributes:
        islocal: N