Summary for clinicians: ERS guidelines on pulmonary alveolar proteinosis.

Pulmonary alveolar proteinosis (PAP) is a rare lung disease caused by accumulation of surfactant in the alveoli, leading to debilitating respiratory symptoms and impaired gas exchange. The recent European Respiratory Society guidelines provide evidence-based recommendations for its diagnosis and man...

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Publicado en:Breathe Vol. 21; no. 2; pp. 1 - 13
Autores principales: Alfaro O., Tiago, McCarthy, Cormac, Bonella, Francesco, Bendstrup, Elisabeth, O'Callaghan, Marissa
Formato: diagnostic images practice guidelines tables/charts Journal Article
Publicado: European Respiratory Society Apr2025
Acceso en línea:Ver este registro en EBSCOhost
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      dt: Apr2025
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      pub: European Respiratory Society
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        atl: Summary for clinicians: ERS guidelines on pulmonary alveolar proteinosis.
      aug:
        au:
          Alfaro O., Tiago
          McCarthy, Cormac
          Bonella, Francesco
          Bendstrup, Elisabeth
          O'Callaghan, Marissa
        affil: Pneumology Unit, Unidade Local de Saúde de Coimbra, Coimbra, Portugal
      sug:
        subj:
          Pulmonary Alveolar Proteinosis Diagnosis
          Pulmonary Alveolar Proteinosis Therapy
          Lung Diseases Diagnosis
          Lung Diseases Therapy
          Medical Practice, Evidence-Based
          Autoimmune Diseases
          Granulocyte-Macrophage Colony-Stimulating Factor
          Autoantibodies
          Bronchoalveolar Lavage
          Rituximab Therapeutic Use
          Plasmapheresis
          Lung Transplantation
      ab: Pulmonary alveolar proteinosis (PAP) is a rare lung disease caused by accumulation of surfactant in the alveoli, leading to debilitating respiratory symptoms and impaired gas exchange. The recent European Respiratory Society guidelines provide evidence-based recommendations for its diagnosis and management. Autoimmune PAP (aPAP) is the most common form, driven by granulocyte-macrophage colony-stimulating factor (GM-CSF) autoantibodies. Recommended diagnostic tools include bronchoalveolar lavage and quantitative GM-CSF antibody testing. Whole lung lavage and inhaled GM-CSF are first-line treatments for symptomatic or progressive aPAP. Rituximab, plasmapheresis, and lung transplantation are options for refractory disease. Referral to expert centres is advised for diagnostic and therapeutic guidance. This case-based summary for clinicians highlights the best clinical approach to patients with suspicion or confirmation of PAP.
      pubtype: Academic Journal
      doctype:
        diagnostic images
        practice guidelines
        tables/charts
        Journal Article
      ougenre: Article
    language: English
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