An overview of the impact of rare disease characteristics on research methodology.
Background: About 30 million individuals in the United States are living with a rare disease, which by definition have a prevalence of 200,000 or fewer cases in the United States ([National Organization for Rare Disorders], [About NORD], [2016]). Disease heterogeneity and geographic dispersion add t...
| Published in: | Orphanet Journal of Rare Diseases Vol. 13; pp. 1 - 13 |
|---|---|
| Main Authors: | , , |
| Format: | research Journal Article |
| Published: |
BioMed Central
1/19/2018
|
| Online Access: | View this record in EBSCOhost |