Predicting study duration in clinical trials with a time-to-event endpoint.

In event-driven clinical trials comparing the survival functions of two groups, the number of events required to achieve the desired power is usually calculated using the Freedman formula or the Schoenfeld formula. Then, the sample size and the study duration derived from the required number of even...

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Publicado en:Statistics in Medicine Vol. 40; no. 10; pp. 2413 - 2422
Autores principales: Machida, Ryunosuke, Fujii, Yosuke, Sozu, Takashi
Formato: research Journal Article
Publicado: Wiley-Blackwell 5/10/2021
Acceso en línea:Ver este registro en EBSCOhost
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      dt: 5/10/2021
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      pub: Wiley-Blackwell
      place: Malden, Massachusetts
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        10.1002/sim.8911
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        atl: Predicting study duration in clinical trials with a time-to-event endpoint.
      aug:
        au:
          Machida, Ryunosuke
          Fujii, Yosuke
          Sozu, Takashi
        affil: Department of Information and Computer Technology, Tokyo University of Science Graduate School of Engineering, Tokyo, Japan
      sug:
        subj:
          Study Design
          Uncertainty
          Human
          Sample Size
          Comparative Studies
          Multicenter Studies
          Evaluation Research
          Validation Studies
          Scales
      ab: In event-driven clinical trials comparing the survival functions of two groups, the number of events required to achieve the desired power is usually calculated using the Freedman formula or the Schoenfeld formula. Then, the sample size and the study duration derived from the required number of events are considered; however, their combination is not uniquely determined. In practice, various combinations are examined considering the enrollment speed, study duration, and the cost of enrollment. However, effective methods for visually representing their relationships and evaluating the uncertainty in study duration are insufficient. We developed a graphical approach for examining the relationship between sample size and study duration. To evaluate the uncertainty in study duration under a given sample size, we also derived the probability density function of the study duration and a method for updating the probability density function according to the observed number of events (ie, information time). The proposed methods are expected to improve the operation and management of clinical trials with a time-to-event endpoint.
      pubtype: Academic Journal
      doctype:
        research
        Journal Article
      ougenre: Article
    language: English
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