How to Balance Prognostic Factors in Controlled Phase II Trials: Stratified Permuted Block Randomization or Minimization? An Analysis of Clinical Trials in Digestive Oncology.

In controlled phase II trials, major prognostic factors need to be well balanced between arms. The main procedures used are SPBR (Stratified Permuted Block Randomization) and minimization. First, we provide a systematic review of the treatment allocation procedure used in gastrointestinal oncology c...

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Publicado en:Current Oncology Vol. 31; no. 6; pp. 3513 - 3529
Autores principales: Martin, Elodie, Le Malicot, Karine, Guérin-Charbonnel, Catherine, Bocquet, François, Bouché, Olivier, Turpin, Anthony, Aparicio, Thomas, Legoux, Jean-Louis, Dahan, Laetitia, Taieb, Julien, Lepage, Côme, Dourthe, Louis-Marie, Pétorin, Caroline, Bourgeois, Vincent, Raoul, Jean-Luc, Seegers, Valérie
Formato: Journal Article
Publicado: MDPI Jun2024
Acceso en línea:Ver este registro en EBSCOhost
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        atl: How to Balance Prognostic Factors in Controlled Phase II Trials: Stratified Permuted Block Randomization or Minimization? An Analysis of Clinical Trials in Digestive Oncology.
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          Martin, Elodie
          Le Malicot, Karine
          Guérin-Charbonnel, Catherine
          Bocquet, François
          Bouché, Olivier
          Turpin, Anthony
          Aparicio, Thomas
          Legoux, Jean-Louis
          Dahan, Laetitia
          Taieb, Julien
          Lepage, Côme
          Dourthe, Louis-Marie
          Pétorin, Caroline
          Bourgeois, Vincent
          Raoul, Jean-Luc
          Seegers, Valérie
        affil: Institut de Cancérologie de l'Ouest, F 49055 Angers, France
      sug:
      ab: In controlled phase II trials, major prognostic factors need to be well balanced between arms. The main procedures used are SPBR (Stratified Permuted Block Randomization) and minimization. First, we provide a systematic review of the treatment allocation procedure used in gastrointestinal oncology controlled phase II trials published in 2019. Second, we performed simulations using data from six phase II studies to measure the impacts of imbalances and bias on the efficacy estimations. From the 40 articles analyzed, all mentioned randomization in both the title and abstract, the median number of patients included was 109, and 77.5% were multicenter. Of the 27 studies that reported at least one stratification variable, 10 included the center as a stratification variable, 10 used minimization, 9 used SBR, and 8 were unspecified. In real data studies, the imbalance increased with the number of centers. The total and marginal imbalances were higher with SBR than with minimization, and the difference increased with the number of centers. The efficiency estimates per arm were close to the original trial estimate in both procedures. Minimization is often used in cases of numerous centers and guarantees better similarity between arms for stratification variables for total and marginal imbalances in phase II trials.
      pubtype: Academic Journal
      doctype: Journal Article
      ougenre: Article
    language: English
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