Perceived Impact on the Daily Lives of Patients With Spinal Muscular Atrophy Treated With Nusinersen: A Natural Language Processing Approach.

Objective: Spinal muscular atrophy (SMA) is a rare neuromuscular disorder caused by SMN1 mutations, leading to progressive muscle weakness. Although nusinersen improves motor function, its broader impact on daily life remains insufficiently understood. This study explored caregivers' perceptions of...

Descripción completa

Detalles Bibliográficos
Publicado en:American Journal of Physical Medicine & Rehabilitation Vol. 105; no. 7; pp. 597 - 603
Autores principales: Castellar-Leones, Sandra, Ruiz-Ospina, Edicson, Correa-Arrieta, Cristian, Ortiz-Corredor, Fernando
Formato: research tables/charts Journal Article
Publicado: Lippincott Williams & Wilkins Jul2026
Acceso en línea:Ver este registro en EBSCOhost