Perceived Impact on the Daily Lives of Patients With Spinal Muscular Atrophy Treated With Nusinersen: A Natural Language Processing Approach.
Objective: Spinal muscular atrophy (SMA) is a rare neuromuscular disorder caused by SMN1 mutations, leading to progressive muscle weakness. Although nusinersen improves motor function, its broader impact on daily life remains insufficiently understood. This study explored caregivers' perceptions of...
| Publicado en: | American Journal of Physical Medicine & Rehabilitation Vol. 105; no. 7; pp. 597 - 603 |
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| Autores principales: | , , , |
| Formato: | research tables/charts Journal Article |
| Publicado: |
Lippincott Williams & Wilkins
Jul2026
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| Acceso en línea: | Ver este registro en EBSCOhost |